Genome therapy of myotonic dystrophy type 1 iPS cells for development of autologous stem cell therapy

Gao Y, Guo X, Santostefano KE, Wang Y. Reid T, Zeng D, Terada N, Ashizawa T, Xia G. Mol. Ther. 24:1378-87, Aug, 2016 PMID: 27203440

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Email: hirnec@coh.org